Talha Badar: New Data on Asciminib in Relapsed/Refractory Ph+ ALL and LBC-CML
Talha Badar/X

Talha Badar: New Data on Asciminib in Relapsed/Refractory Ph+ ALL and LBC-CML

Talha Badar, Hematology/Oncology Specialist at Mayo Clinic, shared a post on X about a recent article by Mathilde Chanut et al, published in Blood Advances

“New data on asciminib in relapsed/refractory Ph+ ALL and lymphoid blast crisis CML (LBC-CML)!

Published in Blood Advances (July 2025).

1) Dose 200 mg BID

2) 93% previously on ponatinib

27/35 had BCR::ABL1 mutations

  • 18 with T315I
  • 8 with compound mutations

3) Responses

  • 36 evaluable patients → 83% achieved CR/CRi
  • Of 23 with MRD data: 57% reached MRD negativity (<0.01% BCR::ABL1)

4) Survival

  • Median OS: ~9.8 months
  • Median EFS: ~4.9 months
  • Longer EFS with combinations vs monotherapy (7.9 vs 4.2 months)”

Title: Asciminib for relapsed or refractory Philadelphia chromosome–positive acute lymphoblastic leukemia

Authors: Mathilde Chanut, Aurélie Cabannes-Hamy, Marie Balsat, Nassim Sahki, Emmanuel Raffoux, Yosr Hicheri, Bruno Lioure, Lucie Laemmel, Thibaut Leguay, Victoria Cacheux, Maria Pilar Gallego-Hernanz, Andrea Pieragostini, Gabrielle Roth-Guepin, Ludovic Gabellier, Nathalie Denizon, Lise Willems, Quentin Cabrera, Sylvain Chantepie, Valérie Coiteux, Claudie Capdupuy, Martin Carré, Antoine Machet, Juliette Lambert, Sandrine Roux, Franck-Emmanuel Nicolini, Nicolas Boissel, Emmanuelle Clappier, Rathana Kim, Philippe Rousselot

Read the Full Article on Blood Advances

Talha Badar: New Data on Asciminib in Relapsed/Refractory Ph+ ALL and LBC-CML

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