Simone Cesaro, Director of Pediatric Hematology Oncology Unit at Integrated University Hospital of Verona, shared on LinkedIn:
“The unsolved problem for pediatric oncology is the limited and delayed access to innovative drugs, so that the off-label or compassionate uses are often the main way to offer new options of treatment to the patients, but it is a continous, day by day, fight against burocracy and regulations.”
Title: Access to innovative therapies outside clinical trials in pediatric oncology: a national real-world analysis of off-label and compassionate use of targeted therapies and immunotherapies
Authors: Valeria Ceolin, Luca Bergamaschi, Federico Mercolini, Daniela Di Carlo, Enrico Opocher, Virginia Livellara, Franco Locatelli, Maria Giuseppina Cefalo, Maria Grazia Pionelli, Carmelo Rizzari, Sofia Arnaboldi, Veronica Leoni, Simone Cesaro, Alberto Romano, Antonio Ruggiero, Luisa Di Pasquale, Luca Lo Nigro, Elisa Coassin, Daniela Onofrillo, Camilla Rosa, Francesca Introzzi, Simona Rinieri, Rossella Mura, Letizia Brescia, Loredana Amoroso, Giovanna Sironi, Silvia Sorbara, Nicoletta Bertorello, Michela Casanova, Franca Fagioli
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